Service and special activities

Presentations on national/international meetings, teaching on webinars about diagnosis and treatment of inborn errors of metabolism

1. Hot topic Hyperphenylalaninemia’s (HPA)

  • differential diagnosis of HPA
  • BH4 (tetrahydrobiopterin) sensitive HPA, neonatal BH4 loading
  • treatment of phenylketonuria (especially BH4)
  • maternal phenylketonuria

2. The patient with unknown diagnosis

  • Database focused research
  • Extended metabolic disgnostic (beside of whole exon sequencing) using GC/MS, NMR, UPLC/MS, high resolution MS

3. Development/support of studies related to inborn errors of metbolism (current own projects)

  • Neonatal BH4 loading in 500 patients with HPA
  • Genotype/Phenotype correlation in HPA
  • Outcome of adult PKU patients: neurotransmitter and other CSF findings
  • Selective screening of patients with a suspected metabolic disease using NMR and UPLC/MS (5000 urine samples)
  • Development of an automatic NMR analysis using www.metagene.de

4. Other activities

  • Support of patient societies like DIG PKU
  • Individual patient support (no treatment advice!) with a possible inborn error of metabolism
  • Participation in ethical commtttee of the State of Baden-Württmeberg